FDA Looks to Bring New Scientific, Consumer Voices to Advisory Committees
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. The FDA is recruiting to fill vacancies on its advisory committees, informally known as adcomms. While these committees have met less frequently during the Trump administration, […]
Mirum Pharma Pill Lands FDA Approval for Ultra-Rare Bone Growth Disorder
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Mirum Pharmaceuticals’ Atebrioz is the third FDA-approved drug for fibrodysplasia ossificans progressiva (FOP), but it brings advantages over the two other products for this rare disease […]
When AI Gets Medicine Wrong, Who’s Liable?
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. As AI technology in healthcare becomes more deeply involved in the complex, high-stakes tasks of diagnosis and treatment planning, traditional lines of accountability will become less […]
Proven Ultragenyx Therapy Is A Life Changing Sanfilippo Fix
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Ultragenyx Pharmaceutical’s Fayuvi is now the first FDA-approved therapy for the underlying cause of Sanfilippo syndrome type A, an ultra-rare inherited neurological disorder. It’s the second […]
Scholar Rock Secures Proven FDA Approval for Rare Disease Drug
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Scholar Rock’s Isembyld isn’t the only FDA-approved therapy for spinal muscular atrophy, but it is the first one that directly targets muscle tissue. Isembyld is the […]