FDA Looks to Bring New Scientific, Consumer Voices to Advisory Committees
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. The FDA is recruiting to fill vacancies on its advisory committees, informally known as adcomms. While these committees have met less frequently during the Trump administration, […]
Mirum Pharma Pill Lands FDA Approval for Ultra-Rare Bone Growth Disorder
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Mirum Pharmaceuticals’ Atebrioz is the third FDA-approved drug for fibrodysplasia ossificans progressiva (FOP), but it brings advantages over the two other products for this rare disease […]
Gene Silencing-Biotech ADARx Makes Some Noise With $535M Stock Market Debut
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. ADARx Pharmaceuticals upsized its IPO and raised additional cash through a private placement with partner AbbVie. Lead ADARx program onvuzosiran is in Phase 3 testing for […]
Electra Lands $350M for Powerful Immunology Drugs
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Electra Therapeutics’ IPO cash will support a potential first-in-class drug whose lead indication is a rare hyperinflammatory disorder with no FDA-approved treatments. Meanwhile, clinical-stage biotechs Marea […]
Telix Secures A Powerful $1.65B Acquisition Deal
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Telix Pharmaceuticals is acquiring Isotope Technologies Munich, or ITM, in a $1.65 billion stock deal that will create a radiopharmaceuticals company with greater global scale. ITM’s […]
New Roche Drug Shows Powerful Results for Kidney Disease
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Roche reported the drug sefaxersen achieved statistically significant and clinically meaningful results in a Phase 3 test in immunoglobulin A nephropathy, or IgAN. This antisense oligonucleotide, […]
Proven Ultragenyx Therapy Is A Life Changing Sanfilippo Fix
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Ultragenyx Pharmaceutical’s Fayuvi is now the first FDA-approved therapy for the underlying cause of Sanfilippo syndrome type A, an ultra-rare inherited neurological disorder. It’s the second […]
Scholar Rock Secures Proven FDA Approval for Rare Disease Drug
đź“° Curated Industry Article This is a summary of a full article from a trusted healthcare and insurance publication. Click “Read Full Article” below to read the complete story. Scholar Rock’s Isembyld isn’t the only FDA-approved therapy for spinal muscular atrophy, but it is the first one that directly targets muscle tissue. Isembyld is the […]